First Press Release


Second Press Release


Fourth Discretionary Advisory  Committee on Heritable Diseases in Newborns and Children,  DACHDNC


Public meeting on Patient-Focused Drug Development for Neurological Manifestations of Inborn Errors of Metabolism


FDA, Division of Gastroenterology & Inborn Error Products, meeting, September 29, 2014


The FDA approved the use of cholic acid for peroxisomal disorders today, 3/17/15


Pilot Study of DHA-EE


Awake Not the Hungry  Published!


Congratulations to Alex and Ana Paula for graduating from Middle School (See Families Page, Ana Paula and Alex Case History).