News

First Press Release

Second Press Release

Fourth Discretionary Advisory  Committee on Heritable Diseases in Newborns and Children,  DACHDNC, meeting

Public meeting on Patient-Focused Drug Development for Neurological Manifestations of Inborn Errors of Metabolism

FDA, Division of Gastroenterology & Inborn Error Products, meeting, September 29, 2014

The FDA approved the use of cholic acid for peroxisomal disorders today, 3/17/15  http://www.fda.gov/NewsEvents/Newsroom/PressAnnouncements/ucm438572.htm

Pilot Study of DHA-EE

Awake Not the Hungry  Published!

Congratulations to Alex and Ana Paula for graduating from Middle School (See Families Page, Ana Paula and Alex Case History).

 

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